FDA Approves First Treatment Targeting Hunter Syndrome Brain Effects

FDA Approves drug for Neurologic Symptoms of Hunter Syndrome - BioPatrika

FDA Approves Avlayah Drug to Treat Neurologic Manifestations of Hunter Syndrome The U.S. Food and Drug Administration approved Avlayah (tividenofusp alfa-eknm) to treat certain individuals with Hunter syndrome (Mucopolysaccharidosis type II or MPS II). “Today is a milestone day for children and their families battling Hunter syndrome,” said FDA Commissioner Marty Makary, M.D., M.P.H. “The […] The post FDA Approves drug for Neurologic Symptoms of…

FDA Approves First Treatment Targeting Hunter Syndrome Brain Effects

WASHINGTON, D.C. — Children with a rare genetic disorder that affects the brain and body will have access to a newly approved treatment designed to slow disease progression, federal regulators announced. What This Means for You Families affected by Hunter syndrome now have a treatment targeting brain-related symptoms The drug may slow disease progression if started early in young children Approval was accelerated, meaning further studies are st…