This Biotech Lets Rare-Disease Families Invest In Its Gene Therapy

This Biotech Lets Rare-Disease Families Invest In Its Gene Therapy

Rare-disease families can now invest in Mahzi Therapeutics' gene therapy, giving patients a financial stake in developing treatments for their own communities

Rare-Disease Families Can Now Invest In Biotech Gene Therapy

A grandfather playing with his grandson in a wheelchair due to a genetic disability of Pitt-Hopkins syndrome . getty In drug development, patients are the people a therapy is for. They enroll, they wait, they hope. What they almost never do is own a stake in the company racing to treat them. Yael Weiss built Mahzi Therapeutics to break that rule. Her clinical-stage biotech develops gene therapies for rare neurodevelopmental disorders, and it is …