Dynamically Covalent Lipid Nanoparticles Mediate CRISPR-Cas9 Genome Editing against Choroidal Neovascularization in Mice
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Dynamically Covalent Lipid Nanoparticles Mediate CRISPR-Cas9 Genome Editing against Choroidal Neovascularization in Mice
Dynamically covalent lipid nanoparticles were engineered to mediate vascular endothelial growth factor A (VEGFA) gene editing and choroidal neovascularization treatment by codelivering Cas9 mRNA and single guide RNA targeting VEGFA. [Science Advances] Full Article
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