Texas Woman Goes to a Hospital for Help with Pain Related to Sickle Cell Anemia, only to Be Told ‘Seems Like You’re Trying to Get High’

Texas woman goes to a hospital for help with pain related to Sickle Cell Anemia, only to be told ‘seems like you’re trying to get high’

She was in pain but still had time to school him.

FDA Approves First Gene Therapy for Young Children with Sickle Cell Disease

The U.S. Food and Drug Administration today issued a supplemental approval for Casgevy (exagamglogene autotemcel) for patients aged 2 years and older with either sickle cell disease (SCD) with recurrent vaso-occlusive crises (VOCs) or transfusion-dependent β thalassemia (TDT).

Children’s Hospital Los Angeles Studies New Gene-Editing Approach for Sickle Cell Disease

Children’s Hospital Los Angeles is participating in RESTORE, an early-stage clinical trial studying an investigational CRISPR-Cas9 therapy designed to directly modify the beta-globin gene in sickle cell disease.