See every side of every news story
Get Started
SubscribeLogin
Israel-Hamas Conflict
Tariffs
Liberation Day
Donald Trump
Natural Disasters
Trade War
Social Media
Stock Markets
Trade
Taxes
Climate Change
Artificial Intelligence
Nintendo
Published • loading... • Updated

BioMarin Seeks Label Expansion For Palynziq After Positive Phase 3 Results In Adolescent Patients - Biomarin Pharmaceutical (NASDAQ:BMRN)

Summary by Benzinga
BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) released topline data from the Phase 3 PEGASUS trial evaluating Palynziq (pegvaliase-pqpz) compared to diet alone in 55 adolescents aged 12-17 with phenylketonuria (PKU). PKU is a rare, inherited metabolic disorder that prevents the body from breaking down the amino acid phenylalanine. Untreated phenylketonuria can lead to brain damage, intellectual disabilities, behavioral symptoms or seizures. The pri…

3 Articles

All
Left
Center
1
Right
BenzingaBenzinga
Center

BioMarin Seeks Label Expansion For Palynziq After Positive Phase 3 Results In Adolescent Patients - Biomarin Pharmaceutical (NASDAQ:BMRN)

BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) released topline data from the Phase 3 PEGASUS trial evaluating Palynziq (pegvaliase-pqpz) compared to diet alone in 55 adolescents aged 12-17 with phenylketonuria (PKU). PKU is a rare, inherited metabolic disorder that prevents the body from breaking down the amino acid phenylalanine. Untreated phenylketonuria can lead to brain damage, intellectual disabilities, behavioral symptoms or seizures. The pri…

·New York, United States
Read Full Article
theweekenddrive.comtheweekenddrive.com
Reposted by
statesmanexaminer.comstatesmanexaminer.com

BioMarin Announces Positive Pivotal Data for PALYNZIQ® (pegvaliase-pqpz) in Adolescents with Phenylketonuria

Company plans to submit for regulatory approval later this year

Read Full Article
Think freely.Subscribe and get full access to Ground NewsSubscriptions start at $9.99/yearSubscribe

Bias Distribution

  • 100% of the sources are Center
100% Center
Factuality

To view factuality data please Upgrade to Premium

Ownership

To view ownership data please Upgrade to Vantage

theweekenddrive.com broke the news in on Wednesday, April 2, 2025.
Sources are mostly out of (0)

Similar News Topics

Diet

Diet

You have read out of your 5 free daily articles.

Join us as a member to unlock exclusive access to diverse content.

News
For You
SearchBlindspotLocal