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Bill provides access to customized gene therapies, medicines
A new bill would allow patients with life-threatening diseases to access customized gene therapies and medicines when no approved options are available.
The Right to Try for Individualized Treatments Act, sponsored by House members from Arizona and Tennessee, offers a pathway to individualized investigational treatments.
The bill defines individualized investigational treatments as drugs or biological products based on a patient's unique genomic profile.
Kendra Riley said under this bill, families like hers would not have needed to move abroad for treatment, giving rare-disease patients a chance before irreversible loss.