Baby with Rare Disease Thrives After Life-Saving World-First Gene Therapy Made by Nobel Laureate, Descendant of Armenian Genocide Survivor

HOUSTON – A Venezuelan mother in Houston struggles for her daughter’s health, diagnosed with a rare disease that affects about 200 people around the world. The suffering has caused her daughter to stop walking, talking and has almost lost her ability to eat. Zoranni is 20 years old, but since she was 8 years old, her life has changed completely: to run and play with other children, her mobility and her voice has gone out. Today she’s in a wheelc…

Eight-year-old Matic from Škofja Loka, who suffers from a rare genetic disease, received gene therapy treatment in the United States on Tuesday. Matic is feeling great after the treatment, and his family is overjoyed, the Viljem Julijan Society announced today. A fundraising campaign recently raised a good 2.1 million euros for his treatment.

Baby with Rare Disease Thrives After Life-Saving World-First Gene Therapy Made by Nobel Laureate, Descendant of Armenian Genocide Survivor

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him, reports the Associated Press.Researchers described the case in a new study, saying he’s among the first to be successfully treated with a custom therapy that seeks to fix a tiny but critical error in his genetic code that kills half of affected infants. Though it may be a while before similar perso…